Preferred Label : atidarsagene autotemcel;
UNII : EPP8G99QG4;
Origin ID : C000731759;
ATC code(s)
- Currated CISMeF NLP mapping
- MeSH term(s) associated for indexing
- Record concept(s)
- Validated automatic mappings to BTNT
https://www.has-sante.fr/jcms/p_3602613/fr/libmeldy-atidarsagene-autotemcel-leucodystrophie-metachromatique-30-mois-6-ans
2025
false
false
false
France
insurance, health, reimbursement
treatment outcome
infant
child
Atidarsagene Autotemcel
atidarsagene autotemcel
gene therapy
infusions, intravenous
leukodystrophy, metachromatic, juvenile
ARSA Gene Mutation
Biallelic Mutation
hematopoietic stem cell transplantation
hematopoietic stem cells
atidarsagene autotemcel
evaluation of the transparency committee
leukodystrophy, metachromatic
---
https://www.has-sante.fr/jcms/p_3702884/fr/libmeldy-atidarsagene-autotemcel-leucodystrophie-metachromatique-30-mois-6-ans
2025
false
false
false
France
atidarsagene autotemcel
evaluation of the transparency committee
---
https://www.has-sante.fr/jcms/p_3555789/fr/libmeldy-atidarsagene-autotemcel-leucodystrophie-metachromatique-ldm
2024
false
false
false
France
Atidarsagene Autotemcel
insurance, health, reimbursement
treatment outcome
gene therapy
arylsulfatase A deficiency
ARSA Gene Mutation
metachromatic leukodystrophy, infant
leukodystrophy, metachromatic, juvenile
child
atidarsagene autotemcel
infusions, intravenous
atidarsagene autotemcel
evaluation of the transparency committee
leukodystrophy, metachromatic
---
https://ansm.sante.fr/tableau-marr/atidarsagene-autotemcel
2023
false
false
false
France
French
guidelines for drug use
pharmacovigilance note
Atidarsagene Autotemcel
risk management
infusions, intravenous
gene therapy
atidarsagene autotemcel
biological products
atidarsagene autotemcel
---
https://www.has-sante.fr/jcms/p_3379875/fr/libmeldy-atidarsagene-autotemcel-leucodystrophie-metachromatique
2022
false
false
false
France
infusions, intravenous
Atidarsagene Autotemcel
leukodystrophy, metachromatic
metachromatic leukodystrophy, infant
leukodystrophy, metachromatic, juvenile
Biallelic Mutation
ARSA Gene
child
summary of product characteristics
package leaflet
immunotherapy, adoptive
guidelines for drug use
atidarsagene autotemcel
evaluation of the transparency committee
---
https://www.has-sante.fr/jcms/p_3263243/fr/libmeldy-population-autologue-enrichie-en-cellules-cd34-qui-contient-des-cellules-souches-progenitrices-hematopoietiques-transduites-ex-vivo-avec-un-vecteur-lentiviral-codant-le-gene-de-l-arylsulfatase-a-humaine
2021
false
false
false
France
genetic therapy
gene therapy
insurance, health, reimbursement
treatment outcome
infusions, intravenous
transplantation, autologous
hematopoietic stem cell transplantation
child
Autologous Hematopoietic Stem Cell Transplantation
leukodystrophy, metachromatic
metachromatic leukodystrophy, infant
leukodystrophy, metachromatic, juvenile
leukodystrophy, metachromatic
atidarsagene autotemcel
evaluation of the transparency committee
hematopoietic stem cells
---
Libmeldy - Autologous CD34 cells encoding ARSA gene
https://www.ema.europa.eu/en/medicines/human/EPAR/libmeldy
2021
false
false
false
Netherlands
French
English
drug evaluation
package leaflet
summary of product characteristics
syndication feed
treatment outcome
drug approval
europe
orphan drug production
product surveillance, postmarketing
gene therapy
child
leukodystrophy, metachromatic
leukodystrophy, metachromatic
mutation
metachromatic leukodystrophy, infant
leukodystrophy, metachromatic, juvenile
ARSA Gene
hematopoietic stem cell transplantation
transplantation, autologous
Cell positive for CD34 antigen (cell)
hematopoietic stem cells
hematopoietic stem cell mobilization
infusions, intravenous
drug evaluation, preclinical
transplantation conditioning
atidarsagene autotemcel
atidarsagene autotemcel
genetic therapy
leukodystrophy, metachromatic
---
https://www.has-sante.fr/jcms/p_3295376/fr/libmeldy-2-10-x-106-cellules/ml-dispersion-pour-perfusion-atidarsagene-autotemcel
https://www.has-sante.fr/jcms/p_3295371/fr/decision-n-2021-0228/dc/sem-du-26-octobre-2021-de-la-presidente-de-la-haute-autorite-de-sante-prise-au-nom-du-college-portant-autorisation-d-acces-precoce-de-la-specialite-libmeldy
2021
false
false
false
France
treatment outcome
Atidarsagene Autotemcel
leukodystrophy, metachromatic
infusions, intravenous
metachromatic leukodystrophy, infant
leukodystrophy, metachromatic, juvenile
rare diseases
gene therapy
leukodystrophy, metachromatic
hematopoietic stem cells
ARSA Gene
orphan drug production
atidarsagene autotemcel
evaluation of the transparency committee
---
