MeSH definition : A functional gene designed for targeted delivery to specific tissues within the body
for correcting or repairing a gene that may be defective.;
A functional gene designed for targeted delivery to specific tissues within the body
for correcting or repairing a gene that may be defective.
https://www.ema.europa.eu/en/medicines/human/EPAR/beqvez 2025 false false false Netherlands French English syndication feed summary of product characteristics package leaflet drug evaluation treatment outcome Fidanacogene Elaparvovec Fidanacogene Elaparvovec fidanacogene elaparvovec drug approval europe Gene Therapy Agents Gene Therapy Agents hemophilia B infusions, intravenous continuity of patient care Infusion-Related Reaction factor IX product surveillance, postmarketing risk management drug interactions Female of Childbearing Potential pregnancy breast feeding drug evaluation, preclinical adult