Preferred Label : Atidarsagene Autotemcel;
UNII : EPP8G99QG4;
NCI Metathesaurus CUI : CL1663424;
Origin ID : C180638;
UMLS CUI : C5556517;
Semantic type(s)
- Cell [UMLS semantic type]
- UMLS correspondences (same concept)
- Validated automatic mappings to BTNT
- concept_is_in_subset
https://www.has-sante.fr/jcms/p_3602613/fr/libmeldy-atidarsagene-autotemcel-leucodystrophie-metachromatique-30-mois-6-ans
2025
false
false
false
France
insurance, health, reimbursement
treatment outcome
infant
child
Atidarsagene Autotemcel
atidarsagene autotemcel
gene therapy
infusions, intravenous
leukodystrophy, metachromatic, juvenile
ARSA Gene Mutation
Biallelic Mutation
hematopoietic stem cell transplantation
hematopoietic stem cells
evaluation of the transparency committee
leukodystrophy, metachromatic
---
https://www.has-sante.fr/jcms/p_3555789/fr/libmeldy-atidarsagene-autotemcel-leucodystrophie-metachromatique-ldm
2024
false
false
false
France
Atidarsagene Autotemcel
insurance, health, reimbursement
treatment outcome
gene therapy
arylsulfatase A deficiency
ARSA Gene Mutation
metachromatic leukodystrophy, infant
leukodystrophy, metachromatic, juvenile
child
atidarsagene autotemcel
infusions, intravenous
evaluation of the transparency committee
leukodystrophy, metachromatic
---
https://ansm.sante.fr/tableau-marr/atidarsagene-autotemcel
2023
false
false
false
France
French
guidelines for drug use
pharmacovigilance note
Atidarsagene Autotemcel
risk management
infusions, intravenous
gene therapy
atidarsagene autotemcel
biological products
---
https://www.has-sante.fr/jcms/p_3379875/fr/libmeldy-atidarsagene-autotemcel-leucodystrophie-metachromatique
2022
false
false
false
France
infusions, intravenous
Atidarsagene Autotemcel
leukodystrophy, metachromatic
metachromatic leukodystrophy, infant
leukodystrophy, metachromatic, juvenile
Biallelic Mutation
ARSA Gene
child
summary of product characteristics
package leaflet
immunotherapy, adoptive
guidelines for drug use
evaluation of the transparency committee
---
https://www.has-sante.fr/jcms/p_3295376/fr/libmeldy-2-10-x-106-cellules/ml-dispersion-pour-perfusion-atidarsagene-autotemcel
https://www.has-sante.fr/jcms/p_3295371/fr/decision-n-2021-0228/dc/sem-du-26-octobre-2021-de-la-presidente-de-la-haute-autorite-de-sante-prise-au-nom-du-college-portant-autorisation-d-acces-precoce-de-la-specialite-libmeldy
2021
false
false
false
France
treatment outcome
Atidarsagene Autotemcel
leukodystrophy, metachromatic
infusions, intravenous
metachromatic leukodystrophy, infant
leukodystrophy, metachromatic, juvenile
rare diseases
gene therapy
leukodystrophy, metachromatic
hematopoietic stem cells
ARSA Gene
orphan drug production
evaluation of the transparency committee
---
