Preferred Label : lumacaftor;

MeSH note : a corrector of CF transmembrane conductance regulator (CTFR); structure in first source;

CISMeF synonym : VX 809; VX809 cpd;

MeSH hyponym : VX-809; VX809;

Is substance : O;

UNII : EGP8L81APK;

Details


Main resources

You can consult :


https://www.has-sante.fr/jcms/p_3471694/fr/orkambi-lumacaftor/ivacaftor-mucoviscidose
2024
false
false
false
France
treatment outcome
insurance, health, reimbursement
lumacaftor, ivacaftor drug combination
drug combinations
ivacaftor
lumacaftor
ivacaftor and lumacaftor
infant
administration, oral
evaluation of the transparency committee
cystic fibrosis

---
https://www.has-sante.fr/jcms/p_3470456/fr/orkambi-lumacaftor/ivacaftor-mucoviscidose-enfant
2023
false
false
false
France
lumacaftor, ivacaftor drug combination
treatment outcome
insurance, health, reimbursement
ivacaftor
lumacaftor
drug combinations
administration, oral
ivacaftor and lumacaftor
Chloride Channel Agonists
cystic fibrosis
CFTR delta F508
guidelines for drug use
evaluation of the transparency committee
infant
cystic fibrosis

---
https://www.has-sante.fr/jcms/p_3109937/fr/orkambi
2019
false
false
false
France
ivacaftor
lumacaftor
administration, oral
treatment outcome
insurance, health, reimbursement
child
cystic fibrosis
cystic fibrosis transmembrane conductance regulator delta F508
mutation
ivacaftor and lumacaftor
evaluation of the transparency committee
lumacaftor, ivacaftor drug combination
drug combinations
quinolones
benzodioxoles
aminophenols
aminopyridines
cystic fibrosis transmembrane conductance regulator

---
https://www.has-sante.fr/portail/jcms/c_2889886/fr/orkambi
https://www.has-sante.fr/portail/jcms/c_2889886/fr/orkambi-lumacaftor-/-ivacaftor-correcteur-et-potentialisateur-du-gene-cftr
2018
false
false
false
France
French
drug combinations
aminophenols
aminopyridines
aminopyridines
aminophenols
quinolones
quinolones
benzodioxoles
benzodioxoles
adolescent
adult
CFTR gene.p.F508 del
cystic fibrosis transmembrane conductance regulator
cystic fibrosis transmembrane conductance regulator delta F508
cystic fibrosis
ivacaftor
ivacaftor
treatment outcome
ivacaftor and lumacaftor
lumacaftor, ivacaftor drug combination
lumacaftor, ivacaftor drug combination
evaluation of the transparency committee
insurance, health, reimbursement
forced expiratory volume
orphan drug production
guidelines for drug use
lumacaftor
lumacaftor
cystic fibrosis transmembrane conductance regulator

---
http://www.has-sante.fr/portail/jcms/c_2656337/fr/orkambi
http://www.has-sante.fr/portail/jcms/c_2656337/fr/orkambi-lumacaftor-/-ivacaftor-correcteur-et-potentialisateur-du-gene-cftr
2016
false
false
false
France
French
drug combinations
aminophenols
aminopyridines
aminopyridines
aminophenols
quinolones
quinolones
benzodioxoles
benzodioxoles
adolescent
adult
CFTR gene.p.F508 del
cystic fibrosis transmembrane conductance regulator
cystic fibrosis transmembrane conductance regulator delta F508
cystic fibrosis
ivacaftor
ivacaftor
treatment outcome
ivacaftor and lumacaftor
lumacaftor, ivacaftor drug combination
lumacaftor, ivacaftor drug combination
evaluation of the transparency committee
insurance, health, reimbursement
forced expiratory volume
guidelines for drug use
orphan drug production
lumacaftor
lumacaftor
cystic fibrosis transmembrane conductance regulator
drug combinations
drug combinations

---
https://www.ema.europa.eu/medicines/human/EPAR/Orkambi
2015
false
false
false
United Kingdom
French
English
summary of product characteristics
package leaflet
drug combinations
aminophenols
aminopyridines
aminopyridines
aminophenols
quinolones
quinolones
benzodioxoles
benzodioxoles
continuity of patient care
adolescent
adult
CFTR gene.p.F508 del
cystic fibrosis transmembrane conductance regulator
cystic fibrosis transmembrane conductance regulator delta F508
cystic fibrosis
ivacaftor
ivacaftor
drug evaluation
syndication feed
drug approval
europe
treatment outcome
pregnancy
breast feeding
drug interactions
drug evaluation, preclinical
product surveillance, postmarketing
ivacaftor and lumacaftor
lumacaftor, ivacaftor drug combination
lumacaftor, ivacaftor drug combination
lumacaftor
lumacaftor
cystic fibrosis transmembrane conductance regulator
drug combinations
drug combinations

---
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07/06/2024


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