Preferred Label : miglustat;

MeSH note : a glucosylceramide synthase inhibitor;

CISMeF synonym : OGT 918; SC 48334; zavesca;

MeSH synonym : n-butyldeoxynojirimycin; n-butyl deoxynojirimycin; N-(n-butyl)deoxy-nojirimycin; N-(n-butyl)deoxynojirimycin; butyldeoxynojirimycin;

MeSH hyponym : SC-48334; OGT-918;

Is substance : O;

UNII : ADN3S497AZ;

InChIKey : UQRORFVVSGFNRO-UTINFBMNSA-N;

Details


Main resources

You can consult :


https://ansm.sante.fr/tableau-acces-derogatoire/miglustat
2023
false
false
false
France
French
miglustat
drug information

---
https://www.has-sante.fr/jcms/p_3470276/fr/pombiliti-cipaglucosidase-alfa-/-opfolda-miglustat-forme-tardive-de-la-maladie-de-pompe
2023
false
false
false
France
Glycogen storage disease type II late onset (disorder)
treatment outcome
insurance, health, reimbursement
drug therapy, combination
enzyme replacement therapy
adult
cipaglucosidase alfa
infusions, intravenous
administration, oral
miglustat
evaluation of the transparency committee
miglustat
glycogen storage disease type ii
Cipaglucosidase Alfa

---
https://www.ema.europa.eu/en/medicines/human/EPAR/opfolda
2023
false
false
false
Netherlands
French
English
treatment outcome
syndication feed
summary of product characteristics
package leaflet
drug evaluation
miglustat
miglustat
miglustat
drug approval
europe
adult
Glycogen storage disease due to acid maltase deficiency, late-onset
adult glycogen storage disease type II
drug therapy, combination
Cipaglucosidase Alfa
administration, oral
capsules
aged
food-drug interactions
pregnancy
breast feeding
drug evaluation, preclinical

---
https://www.has-sante.fr/jcms/p_3456825/fr/pombiliti-cipaglucosidase-alfa-opfolda-miglustat-en-association-forme-tardive-maladie-de-pompe
2023
false
false
false
France
Cipaglucosidase Alfa
cipaglucosidase alfa
Glycogen storage disease type II late onset (disorder)
miglustat
treatment outcome
insurance, health, reimbursement
evaluation of the transparency committee
miglustat
drug therapy, combination
glycogen storage disease type ii

---
https://www.has-sante.fr/jcms/p_3184914/fr/miglustat-dipharma
2020
false
false
false
France
drugs, generic
evaluation of the transparency committee
miglustat
1-Deoxynojirimycin

---
https://www.ema.europa.eu/en/medicines/human/EPAR/miglustat-dipharma
2019
false
false
false
United Kingdom
French
English
treatment outcome
syndication feed
summary of product characteristics
package leaflet
drug evaluation
adult
drugs, generic
drug approval
europe
miglustat
miglustat
gaucher disease, type 1
administration, oral
enzyme inhibitors
enzyme inhibitors
ceramide glucosyltransferase
drug interactions
pregnancy
breast feeding
miglustat
gaucher disease
1-Deoxynojirimycin
1-Deoxynojirimycin
1-Deoxynojirimycin
glucosyltransferases

---
https://www.has-sante.fr/jcms/p_3122215/fr/miglustat-accord
2019
false
false
false
France
miglustat
Niemann-Pick disease, type C
adult
treatment outcome
insurance, health, reimbursement
drugs, generic
administration, oral
child
adolescent
evaluation of the transparency committee
miglustat
1-Deoxynojirimycin

---
https://www.has-sante.fr/jcms/p_3104691/fr/yargesa
2019
false
false
false
France
drugs, generic
miglustat
evaluation of the transparency committee
1-Deoxynojirimycin
1-Deoxynojirimycin

---
https://www.has-sante.fr/jcms/p_3084023/fr/miglustat-dipharma
2019
false
false
false
France
evaluation of the transparency committee
miglustat
1-Deoxynojirimycin

---
https://www.has-sante.fr/portail/jcms/c_2856028/fr/miglustat-gen-orph
2018
false
false
false
false
France
French
evaluation of the transparency committee
miglustat
1-Deoxynojirimycin

---
https://www.has-sante.fr/portail/jcms/c_2891311/fr/miglustat-accord
2018
false
false
false
France
evaluation of the transparency committee
miglustat
1-Deoxynojirimycin

---
https://www.ema.europa.eu/medicines/human/EPAR/miglustat-genorph
2017
false
United Kingdom
French
English
syndication feed
drugs, generic
miglustat
Product containing precisely miglustat 100 milligram/1 each conventional release oral capsule (clinical drug)
gaucher disease, type 1
enzyme inhibitors
europe
enzyme inhibitors
1-Deoxynojirimycin
gaucher disease
administration, oral
adult
treatment outcome
drug interactions
pregnancy
breast feeding
drug approval
miglustat
miglustat
ceramide glucosyltransferase
glucosyltransferases
1-Deoxynojirimycin
glucosyltransferases
package leaflet
drug evaluation
summary of product characteristics
Gaucher disease type 1

---
https://www.ema.europa.eu/medicines/human/EPAR/Yargesa
2017
false
United Kingdom
French
English
syndication feed
drugs, generic
Product containing precisely miglustat 100 milligram/1 each conventional release oral capsule (clinical drug)
Product containing miglustat (medicinal product)
miglustat
gaucher disease, type 1
enzyme inhibitors
1-Deoxynojirimycin
gaucher disease
administration, oral
adult
treatment outcome
drug interactions
pregnancy
breast feeding
drug approval
miglustat
miglustat
ceramide glucosyltransferase
glucosyltransferases
1-Deoxynojirimycin
package leaflet
drug evaluation
summary of product characteristics
Gaucher disease type 1

---
Mise à disposition d'un générique de ZAVESCA
http://www.has-sante.fr/portail/jcms/c_2607073/fr/miglustat-bluefish
2016
false
France
French
English
Product containing precisely miglustat 100 milligram/1 each conventional release oral capsule (clinical drug)
drugs, generic
gaucher disease, type 1
miglustat
administration, oral
miglustat
adult
child
1-Deoxynojirimycin
enzyme inhibitors
treatment outcome
evaluation of the transparency committee
gaucher disease

---
https://www.ema.europa.eu/medicines/human/EPAR/Zavesca
2012
false
United Kingdom
French
English
syndication feed
enzyme inhibitors
1-Deoxynojirimycin
gaucher disease
capsules
administration, oral
orphan drug production
adult
treatment outcome
drug interactions
pregnancy
breast feeding
drug approval
drug labeling
miglustat
miglustat
ceramide glucosyltransferase
glucosyltransferases
1-Deoxynojirimycin
glucosyltransferases
package leaflet
drug evaluation
summary of product characteristics
Gaucher disease type 1

---
http://www.has-sante.fr/portail/upload/docs/application/pdf/2010-01/zavesca_-_ct-7042.pdf
http://www.has-sante.fr/portail/jcms/c_946087/zavesca-miglustat-inhibiteur-de-la-glucosylceramide-synthetase
2009
France
French
miglustat
1-Deoxynojirimycin
orphan drug production
enzyme inhibitors
ceramide glucosyltransferase
glucosyltransferases
Niemann-Pick disease, type C
miglustat
administration, oral
adult
child
treatment outcome
miglustat
enzyme inhibitors
1-Deoxynojirimycin
glucosyltransferases
guidelines for drug use
evaluation of the transparency committee

---
http://www.has-sante.fr/portail/upload/docs/application/pdf/2011-02/zavesca_ct_7042.pdf
http://www.has-sante.fr/portail/upload/docs/application/pdf/2010-01/zavesca_-_ct-7042.pdf
http://www.has-sante.fr/portail/jcms/c_905044/zavesca
2009
false
France
French
English
rare diseases
miglustat
administration, oral
orphan drug production
miglustat
Niemann-Pick disease, type C
adult
child
1-Deoxynojirimycin
enzyme inhibitors
treatment outcome
evaluation of the transparency committee

---
http://www.has-sante.fr/portail/display.jsp?id=c_399915
http://www.has-sante.fr/portail/upload/docs/application/pdf/ct031484.pdf
2003
France
French
capsules
orphan drug production
gaucher disease
glucosyltransferases
ceramide glucosyltransferase
miglustat
administration, oral
treatment outcome
miglustat
1-Deoxynojirimycin
enzyme inhibitors
glucosyltransferases
evaluation of the transparency committee

---
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22/05/2025


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