Preferred Label : olipudase alfa;
Obsolete resource : false;
MeSH Related Number : 6D5766Q4OP;
Registry Number MeSH : EC 3.1.4.12;
UNII : EC 3.1.4.12;
Origin ID : C000608782;
UMLS CUI : C4278198;
ATC code(s)
- Currated CISMeF NLP mapping
- MeSH term(s) associated for indexing
- Record concept(s)
- Semantic type(s)
- UMLS correspondences (same concept)
- Validated automatic mappings to BTNT
https://www.has-sante.fr/jcms/p_3431851/fr/xenpozyme-olipudase-alfa-deficit-en-sphingomyelinase-acide
2023
false
false
false
France
evaluation of the transparency committee
sphingomyelin/cholesterol lipidosis, nos
xenpozyme
acid, nos
olipudase alfa
niemann-pick diseases
olipudase alfa
---
https://www.ema.europa.eu/en/medicines/human/EPAR/xenpozyme
2023
false
false
false
United Kingdom
French
English
treatment outcome
syndication feed
summary of product characteristics
package leaflet
drug evaluation
enzyme replacement therapy
drug approval
europe
olipudase alfa
olipudase alfa
infusions, intravenous
olipudase alfa
Niemann-Pick disease, type B
Niemann-Pick disease, type A
orphan drug production
product surveillance, postmarketing
child
adolescent
adult
pregnancy
breast feeding
drug interactions
drug evaluation, preclinical
---
https://ansm.sante.fr/tableau-acces-derogatoire/xenpozyme#
2023
false
false
false
France
French
drug information
olipudase alfa
olipudase alfa
enzyme replacement therapy
child
adolescent
adult
niemann-pick diseases
---
https://www.has-sante.fr/jcms/p_3456309/fr/xenpozyme-olipudase-alfa-maladie-rare
2023
false
false
false
France
infusions, intravenous
treatment outcome
insurance, health, reimbursement
olipudase alfa
enzyme replacement therapy
child
adult
orphan drug production
Acid sphingomyelinase deficiency
niemann-pick diseases
evaluation of the transparency committee
rare diseases
olipudase alfa
---
https://ansm.sante.fr/tableau-marr/olipudase-alfa
2022
false
false
false
France
French
guidelines for drug use
popular works
risk management
olipudase alfa
olipudase alfa
Drug-Related side effects and adverse reactions
infusions, intravenous
home infusion therapy
Infusion-Related Reaction
drug hypersensitivity
anaphylaxis
olipudase alfa
---
https://www.has-sante.fr/jcms/p_3325559/fr/xenpozyme-olipudase-alfa
https://www.has-sante.fr/jcms/p_3325567/fr/decision-n-2022-0083/dc/sem-du-17-mars-2022-du-college-de-la-haute-autorite-de-sante-portant-autorisation-d-acces-precoce-de-la-specialite-xenpozyme
2022
false
false
false
France
olipudase alfa
insurance, health, reimbursement
treatment outcome
enzyme replacement therapy
child
adolescent
adult
sphingomyelin phosphodiesterase
infusions, intravenous
Acid sphingomyelinase deficiency
olipudase alfa
evaluation of the transparency committee
olipudase alfa
---
https://www.has-sante.fr/jcms/p_3396519/fr/xenpozyme-olipudase-alfa-maladie-rare
2022
false
false
false
France
treatment outcome
insurance, health, reimbursement
olipudase alfa
orphan drug production
enzyme replacement therapy
Acid sphingomyelinase deficiency
Niemann-Pick disease, type A
Niemann-Pick disease, type B
adult
child
infusions, intravenous
evaluation of the transparency committee
olipudase alfa
---
