Preferred Label : Eladocagene Exuparvovec;
NCIt synonyms : Eladocagene Exuparvovec-tneq;
UNII : S51J6N56M7;
CAS number : 2098615-91-7;
Drug name : Kebilidi;
NCI Metathesaurus CUI : CL1405983;
Origin ID : C171796;
UMLS CUI : C5419302;
Semantic type(s)
UMLS correspondences (same concept)
concept_is_in_subset
https://ansm.sante.fr/tableau-acces-derogatoire/upstaza
2025
false
false
false
France
French
Eladocagene Exuparvovec
drug information
infant
Aromatic-L-Amino-Acid decarboxylases
Aromatic-L-Amino-Acid Decarboxylase
aromatic amino acid decarboxylase deficiency
technical report
---
https://ansm.sante.fr/tableau-marr/eladocagene-exuparvovec
2025
false
false
false
France
French
risk management
guidelines for drug use
Eladocagene Exuparvovec
drug compounding
Stereotactic surgery
stereotaxic techniques
gene therapy
Intraputaminal Route of Administration
aromatic amino acid decarboxylase deficiency
Injection of brain (procedure)
infusions, parenteral
neurosurgical procedures
patient education handout
guideline
eladocagene exuparvovec
---
https://www.has-sante.fr/jcms/p_3402378/fr/upstaza-eladocagene-exuparvovec-deficit-en-decarboxylase-d-acide-l-amine-aromatique
2022
false
false
false
France
insurance, health, reimbursement
treatment outcome
child
infant
Eladocagene Exuparvovec
gene therapy
amino acid metabolism, inborn errors
Aromatic-L-Amino-Acid decarboxylases
infusions, parenteral
Intraputaminal Route of Administration
eladocagene exuparvovec
evaluation of the transparency committee
aromatic amino acid decarboxylase deficiency
---
https://www.ema.europa.eu/en/medicines/human/EPAR/upstaza
2022
false
false
false
Netherlands
French
English
treatment outcome
syndication feed
summary of product characteristics
package leaflet
drug evaluation
Eladocagene Exuparvovec
aromatic amino acid decarboxylase deficiency
gene therapy
infant
child
drug approval
europe
amino acid metabolism, inborn errors
infusions, parenteral
Aromatic-L-Amino-Acid decarboxylases
orphan drug production
risk management
product surveillance, postmarketing
adolescent
adult
aromatic amino acid decarboxylase deficiency
genetic testing
Intraputaminal Route of Administration
eladocagene exuparvovec
---