Preferred Label : nulibry;
MeSH note : structure in first source;
CISMeF synonym : cyclic pyranopterin monophosphate;
MeSH Hyperonym : cPMP cpd;
MeSH CAS label : 1,3,2-Dioxaphosphorino(4',5':5,6)pyrano(3,2-g)pteridin-10(4H)-one, 8-amino-4a,5a,6,9,11,11a,12,12a-octahydro-2,12,12-trihydroxy-,
2-oxide, (4aR,5aR,11aR,12aS)-;
Registry Number MeSH : 4X7K2681Y7;
Is substance : O;
Origin ID : C549445;
UMLS CUI : C5443526;
MeSH term(s) associated for indexing
Record concept(s)
Semantic type(s)
https://www.ema.europa.eu/en/medicines/human/EPAR/nulibry
2022
false
false
false
Netherlands
French
English
treatment outcome
syndication feed
summary of product characteristics
package leaflet
drug evaluation
orphan drug production
fosdenopterin
fosdenopterin
nulibry
Product containing only fosdenopterin in parenteral dose form (medicinal product form)
drug approval
europe
molybdenum cofactor deficiency, complementation group A
infusions, intravenous
fosdenopterin
product surveillance, postmarketing
Fosdenopterin Hydrobromide
pregnancy
breast feeding
Replacement Therapy
drug evaluation, preclinical
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