Preferred Label : migalastat;
MeSH note : a potent inhibitor of glycolipid biosynthesis;
CISMeF synonym : 1-deoxy-galactonojirimycin; N-butyldeoxygalacto-nojirimycin;
MeSH hyponym : migalastat HCl;
Related MeSH term : NB-DGJ; N-butyldeoxygalactonojirimycin; 1-deoxygalactonojirimycin; 1-deoxygalacto-nojirimycin;
Is substance : O;
UNII : C4XNY919FW;
InChIKey : LXBIFEVIBLOUGU-DPYQTVNSSA-N;
Origin ID : C090092;
UMLS CUI : C2698220;
Currated CISMeF NLP mapping
MeSH indexing information
MeSH term(s) associated for indexing
Record concept(s)
Semantic type(s)
UMLS correspondences (same concept)
Validated automatic mappings to BTNT
https://www.has-sante.fr/jcms/p_3478088/fr/galafold-chlorhydrate-de-migalastat-deficit-en-a-galactosidase-a
2023
false
false
false
France
fabry disease
adolescent
evaluation of the transparency committee
migalastat hydrochloride
migalastat
Migalastat Hydrochloride
galactosidases
---
https://hpr-rps.hres.ca/reg-content/sommaire-motif-decision-detailTwo.php?lang=fr&linkID=SBD00372
2018
false
false
false
Canada
French
English
drug information
capsules
Adamantinoma
formed
migalastat hydrochloride
administration, oral
migalastat
with shape
1-Deoxynojirimycin
---
http://www.has-sante.fr/portail/jcms/c_2724031/fr/galafold
2016
false
false
false
France
French
evaluation of the transparency committee
administration, oral
treatment outcome
migalastat
migalastat
fabry disease
fabry disease
insurance, health, reimbursement
adult
adolescent
orphan drug production
migalastat
1-Deoxynojirimycin
1-Deoxynojirimycin
1-Deoxynojirimycin
---
https://www.ema.europa.eu/medicines/human/EPAR/Galafold
2016
false
false
false
United Kingdom
French
English
syndication feed
summary of product characteristics
package leaflet
drug evaluation
migalastat
drug approval
europe
treatment outcome
orphan drug production
young adult
adult
fabry disease
continuity of patient care
fabry disease
administration, oral
product surveillance, postmarketing
alpha-Galactosidase
adolescent
mutation
pregnancy
breast feeding
alpha-Galactosidase
drug evaluation, preclinical
migalastat
migalastat
1-Deoxynojirimycin
---
http://www.has-sante.fr/portail/jcms/c_2724031/fr/galafold-migalastat-molecule-chaperon-de-mutations-sensibles-de-l-galactosidase
2016
false
false
false
France
French
evaluation of the transparency committee
guidelines for drug use
treatment outcome
migalastat
adult
alpha-Galactosidase
fabry disease
administration, oral
fabry disease
insurance, health, reimbursement
adolescent
orphan drug production
alpha-Galactosidase
Pharmacological Chaperone
molecular chaperones
migalastat
migalastat
1-Deoxynojirimycin
---