https://www.ema.europa.eu/en/medicines/human/EPAR/pyrukynd 2023 false false false Netherlands French English treatment outcome syndication feed summary of product characteristics package leaflet drug evaluation orphan drug production drug approval europe mitapivat mitapivat mitapivat pyruvate kinase deficiency of red cells administration, oral product surveillance, postmarketing adult drug interactions pregnancy breast feeding drug evaluation, preclinical