Preferred Label : Risdiplam;
MeSH synonym : 7-(4,7-Diazaspiro(2.5)oct-7-yl)-2-(2,8-dimethylimidazo(1,2-b)pyridazin-6-yl)-4H-pyrido(1,2-a)pyrimidin-4-one;
UNII : 76RS4S2ET1;
Origin ID : C000629884;
UMLS CUI : C5139676;
ATC code(s)
Currated CISMeF NLP mapping
MeSH term(s) associated for indexing
Pharmacological action(s)
Record concept(s)
Semantic type(s)
UMLS correspondences (same concept)
Validated automatic mappings to BTNT
https://www.has-sante.fr/jcms/p_3289078/fr/evrysdi-risdiplam
2022
France
evaluation of the transparency committee
Risdiplam
Risdiplam
---
https://cadth.ca/fr/risdiplam
2021
false
false
false
Canada
French
drug information
Risdiplam
azo compounds
pyrimidines
---
https://www.ema.europa.eu/en/medicines/human/EPAR/evrysdi
2021
false
false
false
Netherlands
French
English
treatment outcome
syndication feed
summary of product characteristics
package leaflet
drug evaluation
Risdiplam
Risdiplam
drug approval
europe
administration, oral
muscular atrophy, spinal
child
neuromuscular agents
neuromuscular agents
orphan drug production
risdiplam
drug monitoring
infant
adolescent
adult
pregnancy
breast feeding
drug interactions
fertility
Female of Childbearing Potential
drug evaluation, preclinical
azo compounds
pyrimidines
azo compounds
pyrimidines
---
https://www.has-sante.fr/jcms/p_3289078/fr/evrysdi-0-75-mg/ml-risdiplam
2021
false
false
false
France
treatment outcome
insurance, health, reimbursement
administration, oral
risdiplam
neuromuscular agents
5q spinal muscular atrophy
muscular atrophy, spinal
infant
child
orphan drug production
spinal muscular atrophies of childhood
HMN (Hereditary motor neuropathy) proximal type I
muscular atrophy, spinal, type II
juvenile spinal muscular atrophy
evaluation of the transparency committee
Risdiplam
---
https://ansm.sante.fr/tableau-atu-rtu/risdiplam-0-75-mg-ml-poudre-pour-solution-buvable
2021
false
false
false
France
French
package leaflet
summary of product characteristics
guidelines for drug use
risdiplam
azo compounds
azo compounds
pyrimidines
pyrimidines
administration, oral
neuromuscular agents
neuromuscular agents
5q spinal muscular atrophy
infant
child
spinal muscular atrophies of childhood
Product containing precisely risdiplam 750 microgram/1 milliliter conventional release
oral solution (clinical drug)
Risdiplam
Risdiplam
---
https://www.inesss.qc.ca/thematiques/medicaments/medicaments-evaluation-aux-fins-dinscription/extrait-davis-au-ministre/nom-commercial-a-venir-5707.html
2021
false
false
false
Canada
French
administration, oral
quebec
muscular atrophy, spinal
Risdiplam
Risdiplam
risdiplam
drug evaluation
rare diseases
child
infant
orphan drug production
azo compounds
pyrimidines
azo compounds
pyrimidines
---