https://www.has-sante.fr/jcms/p_3498146/fr/myozyme-alglucosidase-alfa-maladie-de-pompe-deficit-en-glucosidase-acide 2024 false false false France GAA protein, human adult adolescent child treatment outcome insurance, health, reimbursement enzyme replacement therapy infusions, intravenous alglucosidase alfa glycogen storage disease type II, infantile adult glycogen storage disease type II Glycogen storage disease type II late onset (disorder) evaluation of the transparency committee glycogen storage disease type ii alglucosidase alfa