Preferred Label : morpholinos;

MeSH definition : Synthetic analogs of NUCLEIC ACIDS composed of morpholine ring derivatives (MORPHOLINES) linked by phosphorodimidates. One standard DNA nucleic acid base (ADENINE; GUANINE; CYTOSINE; OR THYMINE) is bound to each morpholine ring.;

MeSH synonym : morpholino oligonucleotides; oligonucleotides, morpholino; phosphorodiamidate morpholino oligomers; morpholino oligomers, phosphorodiamidate; oligomers, phosphorodiamidate morpholino; PMO oligomers; oligomers, PMO; MORF oligomers; oligomers, MORF; morpholino oligos; oligos, morpholino; Morpholino; Phosphorodiamidate Morpholino Oligomer; Morpholino Oligomer, Phosphorodiamidate; Oligomer, Phosphorodiamidate Morpholino; Morpholino Oligonucleotide; Oligonucleotide, Morpholino;

Is substance : O;

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Synthetic analogs of NUCLEIC ACIDS composed of morpholine ring derivatives (MORPHOLINES) linked by phosphorodimidates. One standard DNA nucleic acid base (ADENINE; GUANINE; CYTOSINE; OR THYMINE) is bound to each morpholine ring.

https://www.ema.europa.eu/en/medicines/human/EPAR/exondys
2018
false
false
false
United Kingdom
French
English
treatment outcome
syndication feed
summary of product characteristics
package leaflet
drug evaluation
eteplirsen
eteplirsen
eteplirsen
morpholinos
morpholinos

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26/04/2025


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